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From the IDefine CSO: Advancing Gene Replacement Research for Kleefstra Syndrome

person Eric Scheeff
calendar_today Jun 26, 2026

In a new CSO Corner blog post on idefine.org, IDefine Chief Scientific Officer Eric Scheeff, PhD, explains IDefine’s new two-year collaboration with UT Southwestern to explore EHMT1 gene replacement therapy for Kleefstra syndrome, adding another promising preclinical path toward treatment.

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